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Disease Type
Endocrine System
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Genetics
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Genetics
Efficacy and Safety of WTX101 Administered for 48 Weeks Versus Standard of Care in Wilson Disease Subjects
Ages
12 years and older
Gender
Both
Liver
test
Ages
18 years and older
Gender
Both
Endocrine System, Genetics
test
Ages
18 years - 60 years
Gender
Both
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